Antisense oligomers targeted to CAG repeats allow allele-specific knockdown of the gene that causes Huntington's disease.
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Aronin, N. Expanded CAG repeats in the crosshairs. Nat Biotechnol 27, 451–452 (2009). https://doi.org/10.1038/nbt0509-451
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DOI: https://doi.org/10.1038/nbt0509-451